Miglustat in adult and juvenile patients with Niemann-Pick disease type C: Long-term data from a clinical trial Wraith, James E, Vecchio, Darleen, Jacklin, Elizabeth, Abel, Larry, Chadha-Boreham, Harbajan, Luzy, Cécile, Giorgino, Ruben and Patterson, Marc C 2010, Miglustat in adult and juvenile patients with Niemann-Pick disease type C: Long-term data from a clinical trial, Molecular Genetics and Metabolism, vol. 99, no. 4, pp. 351-357, doi: 10.1016/j.ymgme.2009.12.006. Attached Files Name Description MIMEType Size Downloads Title Miglustat in adult and juvenile patients with Niemann-Pick disease type C: Long-term data from a clinical trial Author(s) Wraith, James E Vecchio, Darleen Jacklin, Elizabeth Abel, Larry orcid.org/0000-0002-2393-0644 Chadha-Boreham, Harbajan Luzy, Cécile Giorgino, Ruben Patterson, Marc C Journal name Molecular Genetics and Metabolism Volume number 99 Issue number 4 Start page 351 End page 357 Total pages 7 Publisher ACADEMIC PRESS INC ELSEVIER SCIENCE Place of publication United States Publication date 2010-04-01 ISSN 1096-7192 1096-7206 Keyword(s) Science & Technology Life Sciences & Biomedicine Endocrinology & Metabolism Genetics & Heredity Medicine, Research & Experimental Research & Experimental Medicine Niemann-Pick type C Miglustat Long-term Efficacy Safety CHOLESTEROL TRAFFICKING INHIBITOR SACCADES Language eng DOI 10.1016/j.ymgme.2009.12.006 Indigenous content off Field of Research 1103 Clinical Sciences HERDC Research category C1 Refereed article in a scholarly journal Persistent URL http://hdl.handle.net/10536/DRO/DU:30144145 Document type: Journal Article Collections: Faculty of Health School of Medicine Related Links Link Description Connect to published version Go to link with your DU access privileges     Unless expressly stated otherwise, the copyright for items in DRO is owned by the author, with all rights reserved. Versions Version Filter Type Fri, 16 Oct 2020, 07:15:49 EST Sat, 17 Oct 2020, 04:01:23 EST Sat, 17 Oct 2020, 05:06:10 EST Wed, 04 Nov 2020, 08:59:18 EST Wed, 04 Nov 2020, 09:01:13 EST Wed, 04 Nov 2020, 14:55:51 EST Filtered Full Citation counts:   Cited 117 times in TR Web of Science Cited 144 times in Scopus Search Google Scholar Access Statistics: 52 Abstract Views, 0 File Downloads  -  Detailed Statistics Created: Fri, 16 Oct 2020, 07:15:49 EST

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