Miglustat in adult and juvenile patients with Niemann-Pick disease type C: Long-term data from a clinical trial

Wraith, James E, Vecchio, Darleen, Jacklin, Elizabeth, Abel, Larry, Chadha-Boreham, Harbajan, Luzy, Cécile, Giorgino, Ruben and Patterson, Marc C 2010, Miglustat in adult and juvenile patients with Niemann-Pick disease type C: Long-term data from a clinical trial, Molecular Genetics and Metabolism, vol. 99, no. 4, pp. 351-357, doi: 10.1016/j.ymgme.2009.12.006.

Attached Files
Name Description MIMEType Size Downloads

Title Miglustat in adult and juvenile patients with Niemann-Pick disease type C: Long-term data from a clinical trial
Author(s) Wraith, James E
Vecchio, Darleen
Jacklin, Elizabeth
Abel, LarryORCID iD for Abel, Larry orcid.org/0000-0002-2393-0644
Chadha-Boreham, Harbajan
Luzy, Cécile
Giorgino, Ruben
Patterson, Marc C
Journal name Molecular Genetics and Metabolism
Volume number 99
Issue number 4
Start page 351
End page 357
Total pages 7
Publisher ACADEMIC PRESS INC ELSEVIER SCIENCE
Place of publication United States
Publication date 2010-04-01
ISSN 1096-7192
1096-7206
Keyword(s) Science & Technology
Life Sciences & Biomedicine
Endocrinology & Metabolism
Genetics & Heredity
Medicine, Research & Experimental
Research & Experimental Medicine
Niemann-Pick type C
Miglustat
Long-term
Efficacy
Safety
CHOLESTEROL
TRAFFICKING
INHIBITOR
SACCADES
Language eng
DOI 10.1016/j.ymgme.2009.12.006
Indigenous content off
Field of Research 1103 Clinical Sciences
HERDC Research category C1 Refereed article in a scholarly journal
Persistent URL http://hdl.handle.net/10536/DRO/DU:30144145

Document type: Journal Article
Collections: Faculty of Health
School of Medicine
Connect to link resolver
 
Unless expressly stated otherwise, the copyright for items in DRO is owned by the author, with all rights reserved.

Versions
Version Filter Type
Citation counts: TR Web of Science Citation Count  Cited 117 times in TR Web of Science
Scopus Citation Count Cited 144 times in Scopus
Google Scholar Search Google Scholar
Access Statistics: 52 Abstract Views, 0 File Downloads  -  Detailed Statistics
Created: Fri, 16 Oct 2020, 07:15:49 EST

Every reasonable effort has been made to ensure that permission has been obtained for items included in DRO. If you believe that your rights have been infringed by this repository, please contact drosupport@deakin.edu.au.