Long-term miglustat therapy in children with niemann-pick disease type C

Patterson, M C; Vecchio, D; Jacklin, E; Abel, Larry; Chadha-Boreham, H; Luzy, C; Giorgino, R; Wraith, J E

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Long-term miglustat therapy in children with niemann-pick disease type C

journal contribution

posted on 2010-03-01, 00:00 authored by M C Patterson, D Vecchio, E Jacklin, Larry AbelLarry Abel, H Chadha-Boreham, C Luzy, R Giorgino, J E Wraith

Long-term miglustat therapy in children with niemann-pick disease type C

History

Journal

Journal of Child Neurology

Volume

25

Issue

3

Pagination

300 - 305

Publisher

SAGE PUBLICATIONS INC

Location

United States

Publisher DOI

https://doi.org/10.1177/0883073809344222

ISSN

0883-0738

eISSN

1708-8283

Language

English

Author URL

http://gateway.webofknowledge.com/gateway/Gateway.cgi?GWVersion=2&SrcApp=PARTNER_APP&SrcAuth=LinksAMR&KeyUT=WOS:000274849500005&DestLinkType=FullRecord&DestApp=ALL_WOS&UsrCustomerID=a045e4b2bb1f2b747c68c720ec8913b7

Publication classification

C1 Refereed article in a scholarly journal

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Keywords

Science & Technology Life Sciences & Biomedicine Clinical Neurology Pediatrics Neurosciences & Neurology miglustat Niemann-Pick disease type C efficacy safety GALACTOSYL HYDROLASE DEFICIENCY CLINICAL SPECTRUM BRAIN-STEM LACTOSYLCERAMIDE CHOLESTEROL MUTATIONS HE-1 NPC1

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File(s) under permanent embargo

Long-term miglustat therapy in children with niemann-pick disease type C

History

Journal

Volume

Issue

Pagination

Publisher

Location

Publisher DOI

ISSN

eISSN

Language

Author URL

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Keywords

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